A First-in-Human Safety and Efficacy Study of ALN-CFB, a Small Interfering RNA (siRNA) Targeting Complement Factor B, in Adult Participants With Paroxysmal Nocturnal Hemoglobinuria With Persistent Anemia on a C5 Inhibitor

ALN-CFBOngoingRecruitingPhase 1Open NCT07187401 on ClinicalTrials.gov ↗

Population

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Intervention

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Comparator

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