BrAAVe

A Study to Investigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 55 Years of Age With Non-congenital Myotonic Dystrophy Type 1

SAR446268OngoingRecruitingPhase 1Open NCT06844214 on ClinicalTrials.gov ↗

Population

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Intervention

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Comparator

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