Study to Test the Safety and How Well Patients With Severe Hemophilia A Respond to Treatment With BAY 2599023 (DTX 201), a Drug Therapy That Delivers a Healthy Version of the Defective Factor VIII Gene Into the Nucleus of Liver Cells Using an Altered, Non-infectious Virus (AAV) as a "Shuttle"

BAY2599023 (DTX201)OngoingActive not recruitingPhase 1Open NCT03588299 on ClinicalTrials.gov ↗

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NCT03588299 · Trial Tracker · ComplyRx